Antisense oligonucleotide rescue of CGG expansion–dependent FMR1 mis-splicing in fragile X syndrome restores FMRP
出版年份 2023 全文链接
标题
Antisense oligonucleotide rescue of CGG expansion–dependent
FMR1
mis-splicing in fragile X syndrome restores FMRP
作者
关键词
-
出版物
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
Volume 120, Issue 27, Pages -
出版商
Proceedings of the National Academy of Sciences
发表日期
2023-06-27
DOI
10.1073/pnas.2302534120
参考文献
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