标题
Biochemical signatures of disease severity in multiple sulfatase deficiency
作者
关键词
-
出版物
JOURNAL OF INHERITED METABOLIC DISEASE
Volume -, Issue -, Pages -
出版商
Wiley
发表日期
2023-10-23
DOI
10.1002/jimd.12688
参考文献
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Preclinical studies to support the intrathecal delivery of scAAV9/SUMF1 as a gene replacement therapy for multiple sulfatase deficiency
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