Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria

出版年份 2016 全文链接

标题

作者

关键词

Gene therapy, Acute intermittent porphyria, AAV/PBGD, Adeno-associated virus

出版物

Volume 65, Issue 4, Pages 776-783

出版商

Elsevier BV

发表日期

2016-05-18

DOI

10.1016/j.jhep.2016.05.012

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