Real‐life experience with inotersen in hereditary transthyretin amyloidosis with late‐onset phenotype: Data from an early‐access program in Italy

Rate of neuropathic progression in hereditary transthyretin amyloidosis with polyneuropathy and other peripheral neuropathies: a systematic review and meta-analysis

(2021) Xiaochen Lin et al.   BMC Neurology

The neuropathy in hereditary transthyretin amyloidosis : A narrative review

(2021) Stefano Tozza et al.   JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM

Patisiran in hATTR Amyloidosis: Six-Month Latency Period before Efficacy

(2021) Luca Gentile et al.   Brain Sciences

Use of Drugs for ATTRv Amyloidosis in the Real World: How Therapy Is Changing Survival in a Non-Endemic Area

(2021) Massimo Russo et al.   Brain Sciences

Diagnosis and Treatment of Hereditary Transthyretin Amyloidosis (hATTR) Polyneuropathy: Current Perspectives on Improving Patient Care

(2020) Marco Luigetti et al.   Therapeutics and Clinical Risk Management

Early data on long‐term efficacy and safety of inotersen in patients with hereditary transthyretin amyloidosis: a 2‐year update from the open‐label extension of the NEURO‐TTR trial

(2020) T. H. Brannagan et al.   EUROPEAN JOURNAL OF NEUROLOGY

ATTRv amyloidosis Italian Registry: clinical and epidemiological data

(2020) Massimo Russo et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Burden of Hereditary Transthyretin Amyloidosis on Quality of Life

(2019) Aaron Yarlas et al.   MUSCLE & NERVE

Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

(2018) David Adams et al.   NEW ENGLAND JOURNAL OF MEDICINE

Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis

(2018) Merrill D. Benson et al.   NEW ENGLAND JOURNAL OF MEDICINE

Rapid progression of familial amyloidotic polyneuropathy

(2015) David Adams et al.   NEUROLOGY

Repurposing Diflunisal for Familial Amyloid Polyneuropathy

(2015) John L. Berk et al.   JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION

Tafamidis for transthyretin familial amyloid polyneuropathy: A randomized, controlled trial

(2012) T. Coelho et al.   NEUROLOGY

Familial amyloid polyneuropathy

(2011) Violaine Planté-Bordeneuve et al.   LANCET NEUROLOGY