Association between prophylactic angiotensin-converting enzyme inhibitors and overall survival in Duchenne muscular dystrophy—analysis of registry data

Variability and trends in corticosteroid use by male United States participants with Duchenne muscular dystrophy in the Duchenne Registry

(2019) Leslie Cowen et al.   BMC Neurology

Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac, bone health, and orthopaedic management

(2018) David J Birnkrant et al.   LANCET NEUROLOGY

How to estimate the effect of treatment duration on survival outcomes using observational data

(2018)   BMJ-British Medical Journal

How to estimate the effect of treatment duration on survival outcomes using observational data

(2018)   BMJ-British Medical Journal

Using Big Data to Emulate a Target Trial When a Randomized Trial Is Not Available: Table 1.

(2016) Miguel A. Hernán et al.   AMERICAN JOURNAL OF EPIDEMIOLOGY

Effectiveness of Screening Colonoscopy to Prevent Colorectal Cancer Among Medicare Beneficiaries Aged 70 to 79 Years

(2016) Xabier García-Albéniz et al.   ANNALS OF INTERNAL MEDICINE

Specifying a target trial prevents immortal time bias and other self-inflicted injuries in observational analyses

(2016) Miguel A. Hernán et al.   JOURNAL OF CLINICAL EPIDEMIOLOGY

Dystrophin-Deficient Cardiomyopathy

(2016) Forum Kamdar et al.   JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY

Contemporary Cardiac Issues in Duchenne Muscular Dystrophy: Table.

(2015) Elizabeth M. McNally et al.   CIRCULATION

Renal function in children and adolescents with Duchenne muscular dystrophy

(2015) Elke Braat et al.   NEUROMUSCULAR DISORDERS

Oral Corticosteroids and Onset of Cardiomyopathy in Duchenne Muscular Dystrophy

(2013) Brent J. Barber et al.   JOURNAL OF PEDIATRICS

Comparison of methods for estimating the effect of salvage therapy in prostate cancer when treatment is given by indication

(2013) Jeremy M. G. Taylor et al.   STATISTICS IN MEDICINE

Observational data for comparative effectiveness research: An emulation of randomised trials of statins and primary prevention of coronary heart disease

(2011) Goodarz Danaei et al.   STATISTICAL METHODS IN MEDICAL RESEARCH

When to Start Treatment? A Systematic Approach to the Comparison of Dynamic Regimes Using Observational Data

(2010) Lauren E. Cain et al.  

Balance diagnostics for comparing the distribution of baseline covariates between treatment groups in propensity-score matched samples

(2009) Peter C. Austin   STATISTICS IN MEDICINE

Observational Studies Analyzed Like Randomized Experiments

(2008) Miguel A. Hernán et al.   EPIDEMIOLOGY

Effect of deflazacort on cardiac and sternocleidomastoid muscles in Duchenne muscular dystrophy: A magnetic resonance imaging study

(2008) Sophie Mavrogeni et al.   EUROPEAN JOURNAL OF PAEDIATRIC NEUROLOGY

Corticosteroid treatment retards development of ventricular dysfunction in Duchenne muscular dystrophy

(2008) Larry W. Markham et al.   NEUROMUSCULAR DISORDERS

Deflazacort Use in Duchenne Muscular Dystrophy: An 8-Year Follow-Up

(2008) Sylvie Houde et al.   PEDIATRIC NEUROLOGY