Targeting G542X CFTR nonsense alleles with ELX-02 restores CFTR function in human-derived intestinal organoids
出版年份 2021 全文链接
标题
Targeting G542X CFTR nonsense alleles with ELX-02 restores CFTR function in human-derived intestinal organoids
作者
关键词
Read-through, Organoid, Nonsense allele, Cystic fibrosis, ELX-02, NB124
出版物
Journal of Cystic Fibrosis
Volume -, Issue -, Pages -
出版商
Elsevier BV
发表日期
2021-02-06
DOI
10.1016/j.jcf.2021.01.009
参考文献
相关参考文献
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