Formulation and efficacy of ECO/pRHO-ABCA4-SV40 nanoparticles for nonviral gene therapy of Stargardt disease in a mouse model
出版年份 2020 全文链接
标题
Formulation and efficacy of ECO/pRHO-ABCA4-SV40 nanoparticles for nonviral gene therapy of Stargardt disease in a mouse model
作者
关键词
Non-viral gene delivery, ECO, Plasmid DNA, Gene therapy, SV40 enhancer, Stargardt disease
出版物
JOURNAL OF CONTROLLED RELEASE
Volume 330, Issue -, Pages 329-340
出版商
Elsevier BV
发表日期
2020-12-21
DOI
10.1016/j.jconrel.2020.12.010
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