Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria

标题
Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
作者
关键词
-
出版物
NEW ENGLAND JOURNAL OF MEDICINE
Volume 382, Issue 24, Pages 2289-2301
出版商
Massachusetts Medical Society
发表日期
2020-06-11
DOI
10.1056/nejmoa1913147

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