Correction of three prominent mutations in mouse and human models of Duchenne muscular dystrophy by single-cut genome editing

标题
Correction of three prominent mutations in mouse and human models of Duchenne muscular dystrophy by single-cut genome editing
作者
关键词
dystrophin, CRISPR-Cas9, single guide RNA, myopathy, AAV9, human iPSCs
出版物
MOLECULAR THERAPY
Volume -, Issue -, Pages -
出版商
Elsevier BV
发表日期
2020-05-30
DOI
10.1016/j.ymthe.2020.05.024

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