Human liver stem cells express UGT1A1 and improve phenotype of immunocompromised Crigler Najjar syndrome type I mice
出版年份 2020 全文链接
标题
Human liver stem cells express UGT1A1 and improve phenotype of immunocompromised Crigler Najjar syndrome type I mice
作者
关键词
-
出版物
Scientific Reports
Volume 10, Issue 1, Pages -
出版商
Springer Science and Business Media LLC
发表日期
2020-01-21
DOI
10.1038/s41598-020-57820-2
参考文献
相关参考文献
注意：仅列出部分参考文献，下载原文获取全部文献信息。- Phase I/II Trial of Liver Derived Mesenchymal Stem Cells in Pediatric Liver Based Metabolic Disorders
- (2019) Françoise Smets et al. TRANSPLANTATION
- Transplanted Human Pluripotent Stem Cell-Derived Mesenchymal Stem Cells Support Liver Regeneration in Gunn Rats
- (2018) Lucas-Sebastian Spitzhorn et al. STEM CELLS AND DEVELOPMENT
- Repeated AAV-mediated gene transfer by serotype switching enables long-lasting therapeutic levels of hUgt1a1 enzyme in a mouse model of Crigler–Najjar Syndrome Type I
- (2017) L Bočkor et al. GENE THERAPY
- Evaluation of region selective bilirubin-induced brain damage as a basis for a pharmacological treatment
- (2017) Matteo Dal Ben et al. Scientific Reports
- The Intravenous Route of Injection Optimizes Engraftment and Survival in the Murine Model of In Utero Hematopoietic Cell Transplantation
- (2016) Matthew M. Boelig et al. BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION
- Prospects for Adult Stem Cells in the Treatment of Liver Diseases
- (2016) Sharmila Fagoonee et al. STEM CELLS AND DEVELOPMENT
- The RNA-binding protein ESRP1 promotes human colorectal cancer progression
- (2016) Sharmila Fagoonee et al. Oncotarget
- A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome
- (2016) Giuseppe Ronzitti et al. Molecular Therapy-Methods & Clinical Development
- Human induced pluripotent stem cells for monogenic disease modelling and therapy
- (2016) Paola Spitalieri et al. World Journal of Stem Cells
- Human neonatal hepatocyte transplantation induces long-term rescue of unconjugated hyperbilirubinemia in the Gunn rat
- (2015) Laia Tolosa et al. LIVER TRANSPLANTATION
- Recellularization of Rat Liver Scaffolds by Human Liver Stem Cells
- (2015) Victor Navarro-Tableros et al. TISSUE ENGINEERING PART A
- ESRP2 controls an adult splicing programme in hepatocytes to support postnatal liver maturation
- (2015) Amruta Bhate et al. Nature Communications
- Amelioration of Hyperbilirubinemia in Gunn Rats after Transplantation of Human Induced Pluripotent Stem Cell-Derived Hepatocytes
- (2015) Yong Chen et al. Stem Cell Reports
- Age-dependent pattern of cerebellar susceptibility to bilirubin neurotoxicity in vivo in mice
- (2014) G. Bortolussi et al. Disease Models & Mechanisms
- Life-Long Correction of Hyperbilirubinemia with a Neonatal Liver-Specific AAV-Mediated Gene Transfer in a Lethal Mouse Model of Crigler–Najjar Syndrome
- (2014) Giulia Bortolussi et al. HUMAN GENE THERAPY
- Treating inborn errors of liver metabolism with stem cells: current clinical development
- (2014) Etienne Marc Sokal JOURNAL OF INHERITED METABOLIC DISEASE
- Generation of Ugt1-Deficient Murine Liver Cell Lines Using TALEN Technology
- (2014) Fabiola Porro et al. PLoS One
- Human liver stem/progenitor cells decrease serum bilirubin in hyperbilirubinemic Gunn rat
- (2014) Cédric Maerckx WORLD JOURNAL OF GASTROENTEROLOGY
- Human liver stem cells and derived extracellular vesicles improve recovery in a murine model of acute kidney injury
- (2014) Maria Sanchez et al. Stem Cell Research & Therapy
- Monogenic diseases that can be cured by liver transplantation
- (2013) Stefano Fagiuoli et al. JOURNAL OF HEPATOLOGY
- Bilirubin-Induced Neurologic Damage — Mechanisms and Management Approaches
- (2013) Jon F. Watchko et al. NEW ENGLAND JOURNAL OF MEDICINE
- Clinical Outcome of Hepatocyte Transplantation in Four Pediatric Patients with Inherited Metabolic Diseases
- (2012) Carmen Ribes-Koninckx et al. CELL TRANSPLANTATION
- Human liver stem cells improve liver injury in a model of fulminant liver failure
- (2012) Maria Beatriz Herrera et al. HEPATOLOGY
- Rescue of bilirubin-induced neonatal lethality in a mouse model of Crigler-Najjar syndrome type I by AAV9-mediated gene transfer
- (2011) Giulia Bortolussi et al. FASEB JOURNAL
- Validated assay for studying activity profiles of human liver UGTs after drug exposure: inhibition and induction studies
- (2010) M. Teresa Donato et al. ANALYTICAL AND BIOANALYTICAL CHEMISTRY
- Liver transplantation for inherited metabolic disorders of the liver
- (2010) Maryam Moini et al. Current Opinion in Organ Transplantation
- Cell therapy for the diseased liver: from stem cell biology to novel models for hepatotropic human pathogens
- (2008) N. Brezillon et al. Disease Models & Mechanisms
- Treatment of Crigler-Najjar Syndrome Type 1 by Hepatic Progenitor Cell Transplantation: A Simple Procedure for Management of Hyperbilirubinemia
- (2008) A.A. Khan et al. TRANSPLANTATION PROCEEDINGS
- Liver cell transplantation for Crigler-Najjar syndrome type I: Update and perspectives
- (2008) Philippe A Lysy et al. WORLD JOURNAL OF GASTROENTEROLOGY
Find Funding. Review Successful Grants.
Explore over 25,000 new funding opportunities and over 6,000,000 successful grants.
ExploreBecome a Peeref-certified reviewer
The Peeref Institute provides free reviewer training that teaches the core competencies of the academic peer review process.
Get Started