Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis
出版年份 2020 全文链接
标题
Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis
作者
关键词
-
出版物
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
Volume -, Issue -, Pages 1-10
出版商
Informa UK Limited
发表日期
2020-03-05
DOI
10.1080/13506129.2020.1730790
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Effects of Patisiran, an RNA Interference Therapeutic, on Cardiac Parameters in Patients With Hereditary Transthyretin-Mediated Amyloidosis
- (2019) Scott D. Solomon et al. CIRCULATION
- Burden of Hereditary Transthyretin Amyloidosis on Quality of Life
- (2019) Aaron Yarlas et al. MUSCLE & NERVE
- Natural History, Quality of Life, and Outcome in Cardiac Transthyretin Amyloidosis
- (2019) Thirusha Lane et al. CIRCULATION
- Hereditary transthyretin amyloidosis: a model of medical progress for a fatal disease
- (2019) David Adams et al. Nature Reviews Neurology
- Autonomic involvement in hereditary transthyretin amyloidosis (hATTR amyloidosis)
- (2018) Alejandra Gonzalez-Duarte CLINICAL AUTONOMIC RESEARCH
- Symptoms of Autonomic Dysfunction in Systemic Sclerosis Assessed by the COMPASS-31 Questionnaire
- (2018) Brittany L. Adler et al. JOURNAL OF RHEUMATOLOGY
- Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
- (2018) David Adams et al. NEW ENGLAND JOURNAL OF MEDICINE
- Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis
- (2018) Merrill D. Benson et al. NEW ENGLAND JOURNAL OF MEDICINE
- Assessing mNIS+7Ionis and international neurologists' proficiency in a familial amyloidotic polyneuropathy trial
- (2017) Peter J. Dyck et al. MUSCLE & NERVE
- Sixty years of transthyretin familial amyloid polyneuropathy (TTR-FAP) in Europe
- (2016) Yesim Parman et al. CURRENT OPINION IN NEUROLOGY
- “Red-flag” symptom clusters in transthyretin familial amyloid polyneuropathy
- (2016) Isabel Conceição et al. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM
- The Combined Effect of Neuropsychological and Neuropathological Deficits on Instrumental Activities of Daily Living in Older Adults: a Systematic Review
- (2016) Eduard J. Overdorp et al. NEUROPSYCHOLOGY REVIEW
- Hereditary ATTR amyloidosis: a single-institution experience with 266 patients
- (2015) Paul L. Swiecicki et al. AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
- Evolving landscape in the management of transthyretin amyloidosis
- (2015) Philip N. Hawkins et al. ANNALS OF MEDICINE
- Detection of undisclosed neuropathy and assessment of its impact on quality of life: a survey in 25,000 Romanian patients with diabetes
- (2015) Andrei I. Veresiu et al. JOURNAL OF DIABETES AND ITS COMPLICATIONS
- Characterization of Pain in Familial Amyloid Polyneuropathy
- (2015) Sophie Ng Wing Tin et al. JOURNAL OF PAIN
- The Val30Met familial amyloid polyneuropathy specific Rasch-built overall disability scale (FAP-RODS©)
- (2015) Mariëlle H. J. Pruppers et al. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM
- Rapid progression of familial amyloidotic polyneuropathy
- (2015) David Adams et al. NEUROLOGY
- Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study
- (2015) Ole B Suhr et al. Orphanet Journal of Rare Diseases
- Transthyretin Familial Amyloid Polyneuropathy Impact on Health-Related Quality of Life
- (2015) M Inês et al. VALUE IN HEALTH
- Cardiac Findings and Events Observed in an Open-Label Clinical Trial of Tafamidis in Patients with non-Val30Met and non-Val122Ile Hereditary Transthyretin Amyloidosis
- (2015) Thibaud Damy et al. Journal of Cardiovascular Translational Research
- Repurposing Diflunisal for Familial Amyloid Polyneuropathy
- (2015) John L. Berk et al. JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION
- The Relative Impacts of Disease on Health Status and Capability Wellbeing: A Multi-Country Study
- (2015) Paul Mark Mitchell et al. PLoS One
- Norfolk QOL-DN: validation of a patient reported outcome measure in transthyretin familial amyloid polyneuropathy
- (2014) Etta J. Vinik et al. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM
- THAOS: Gastrointestinal manifestations of transthyretin amyloidosis - common complications of a rare disease
- (2014) Jonas Wixner et al. Orphanet Journal of Rare Diseases
- Cardiac amyloidosis: Updates in diagnosis and management
- (2013) Dania Mohty et al. Archives of Cardiovascular Diseases
- Safety and Efficacy of RNAi Therapy for Transthyretin Amyloidosis
- (2013) Teresa Coelho et al. NEW ENGLAND JOURNAL OF MEDICINE
- Guideline of transthyretin-related hereditary amyloidosis for clinicians
- (2013) Yukio Ando et al. Orphanet Journal of Rare Diseases
- Prospective evaluation of the morbidity and mortality of wild-type and V122I mutant transthyretin amyloid cardiomyopathy: The Transthyretin Amyloidosis Cardiac Study (TRACS)
- (2012) Frederick L. Ruberg et al. AMERICAN HEART JOURNAL
- Transthyretin (TTR) Cardiac Amyloidosis
- (2012) Frederick L. Ruberg et al. CIRCULATION
- THAOS – The Transthyretin Amyloidosis Outcomes Survey: initial report on clinical manifestations in patients with hereditary and wild-type transthyretin amyloidosis
- (2012) Teresa Coelho et al. CURRENT MEDICAL RESEARCH AND OPINION
- Disease profile and differential diagnosis of hereditary transthyretin-related amyloidosis with exclusively cardiac phenotype: an Italian perspective
- (2012) C. Rapezzi et al. EUROPEAN HEART JOURNAL
- Cardiac transthyretin amyloidosis
- (2012) Jason N Dungu et al. HEART
- COMPASS 31: A Refined and Abbreviated Composite Autonomic Symptom Score
- (2012) David M. Sletten et al. MAYO CLINIC PROCEEDINGS
- Amyloid Neuropathies
- (2012) Susan C. Shin et al. MOUNT SINAI JOURNAL OF MEDICINE
- Tafamidis for transthyretin familial amyloid polyneuropathy: A randomized, controlled trial
- (2012) T. Coelho et al. NEUROLOGY
- Recent advances in the treatment of familial amyloid polyneuropathy
- (2012) David Adams Therapeutic Advances in Neurological Disorders
- Efficacy and Safety of Antioxidant Treatment With -Lipoic Acid Over 4 Years in Diabetic Polyneuropathy: The NATHAN 1 trial
- (2011) D. Ziegler et al. DIABETES CARE
- Cardiac phenotype and clinical outcome of familial amyloid polyneuropathy associated with transthyretin alanine 60 variant
- (2011) P. T. Sattianayagam et al. EUROPEAN HEART JOURNAL
- Rasch-built Overall Disability Scale (R-ODS) for immune-mediated peripheral neuropathies
- (2011) S. I. van Nes et al. NEUROLOGY
Find Funding. Review Successful Grants.
Explore over 25,000 new funding opportunities and over 6,000,000 successful grants.
ExploreCreate your own webinar
Interested in hosting your own webinar? Check the schedule and propose your idea to the Peeref Content Team.
Create Now