RAINBOWFISH: A study of risdiplam (RG7916) in newborns with pre-symptomatic spinal muscular atrophy (SMA)
NEUROMUSCULAR DISORDERS (2019)
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NEUROMUSCULAR DISORDERS
卷 29, 期 -, 页码 S187-S187出版社
PERGAMON-ELSEVIER SCIENCE LTD
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