4.2 Meeting Abstract

RAINBOWFISH: A study of risdiplam (RG7916) in newborns with pre-symptomatic spinal muscular atrophy (SMA)

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NEUROMUSCULAR DISORDERS
卷 29, 期 -, 页码 S187-S187

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PERGAMON-ELSEVIER SCIENCE LTD
DOI: 10.1016/j.nmd.2019.06.524

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