AAV5-miHTT gene therapy demonstrates sustained huntingtin lowering and functional improvement in Huntington disease mouse models

出版年份 2019 全文链接

标题

作者

关键词

Huntington disease, gene silencing, HD mouse model, gene therapy, therapeutic microRNAs, adeno-associated viral vector serotype 5

出版物

Volume -, Issue -, Pages -

出版商

Elsevier BV

发表日期

2019-03-16

DOI

10.1016/j.omtm.2019.03.002

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