Huntingtin Lowering Strategies for Disease Modification in Huntington’s Disease

标题
Huntingtin Lowering Strategies for Disease Modification in Huntington’s Disease
作者
关键词
Huntington’s disease, genome editing, zinc-finger proteins, transcription activator-like effector nucleases, CRISPR/Cas9, RNAi, antisense oligonucleotides, small-molecule splicing modulators, proteolysis-targeting chimeras, HD biomarkers, drug delivery
出版物
NEURON
Volume 101, Issue 5, Pages 801-819
出版商
Elsevier BV
发表日期
2019-03-07
DOI
10.1016/j.neuron.2019.01.039

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