Twice-weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy

Clinical, Social, and Genetic Factors Associated with Obesity at 12 Months of Age

(2018) Sahel Hazrati et al.   JOURNAL OF PEDIATRICS

Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study

(2018) Craig M McDonald et al.   LANCET

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and neuromuscular, rehabilitation, endocrine, and gastrointestinal and nutritional management

(2018) David J Birnkrant et al.   LANCET NEUROLOGY

Intermittent glucocorticoid steroid dosing enhances muscle repair without eliciting muscle atrophy

(2017) Mattia Quattrocelli et al.   JOURNAL OF CLINICAL INVESTIGATION

Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

(2017) Craig M McDonald et al.   LANCET

Longitudinal effect of eteplirsen versus historical control on ambulation in Duchenne muscular dystrophy

(2016) Jerry R. Mendell et al.   ANNALS OF NEUROLOGY

Clinical trial readiness in non-ambulatory boys and men with duchenne muscular dystrophy: MDA-DMD network follow-up

(2016) Anne M. Connolly et al.   MUSCLE & NERVE

Muscle ultrasound quantifies disease progression over time in infants and young boys with duchenne muscular dystrophy

(2015) Craig M. Zaidman et al.   MUSCLE & NERVE

Characterization of pulmonary function in Duchenne Muscular Dystrophy

(2015) O.H. Mayer et al.   PEDIATRIC PULMONOLOGY

Ataluren treatment of patients with nonsense mutation dystrophinopathy

(2014) Katharine Bushby et al.   MUSCLE & NERVE

Examination of effects of corticosteroids on skeletal muscles of boys with DMD using MRI and MRS

(2014) I. Arpan et al.   NEUROLOGY

One Year Outcome of Boys With Duchenne Muscular Dystrophy Using the Bayley-III Scales of Infant and Toddler Development

(2014) Anne M. Connolly et al.   PEDIATRIC NEUROLOGY

Eteplirsen for the treatment of Duchenne muscular dystrophy

(2013) Jerry R. Mendell et al.   ANNALS OF NEUROLOGY

VBP15, a novel anti-inflammatory and membrane-stabilizer, improves muscular dystrophy without side effects

(2013) Christopher R. Heier et al.   EMBO Molecular Medicine

Motor and cognitive assessment of infants and young boys with Duchenne Muscular Dystrophy: results from the Muscular Dystrophy Association DMD Clinical Research Network

(2013) Anne M. Connolly et al.   NEUROMUSCULAR DISORDERS

Early neurodevelopmental assessment in Duchenne muscular dystrophy

(2013) Marika Pane et al.   NEUROMUSCULAR DISORDERS

Randomized, blinded trial of weekend vs daily prednisone in Duchenne muscular dystrophy

(2011) D. M. Escolar et al.   NEUROLOGY

Contrasting effects of steroids and angiotensin-converting-enzyme inhibitors in a mouse model of dystrophin-deficient cardiomyopathy

(2009) Ralf Bauer et al.   EUROPEAN JOURNAL OF HEART FAILURE

Successful treatment of refractory Langerhans cell histiocytosis by allogeneic peripheral blood stem cell transplantation

(2007) Chi-Chieh Lai et al.   PEDIATRIC TRANSPLANTATION