Antisense oligonucleotide eluforsen improves CFTR function in F508del cystic fibrosis

标题
Antisense oligonucleotide eluforsen improves CFTR function in F508del cystic fibrosis
作者
关键词
Antisense Oligonucleotide, Clinical Trial, Cystic Fibrosis Transmembrane Conductance Regulator delta F508, Nasal Potential Difference, Pulmonary Medicine
出版物
Journal of Cystic Fibrosis
Volume -, Issue -, Pages -
出版商
Elsevier BV
发表日期
2018-11-19
DOI
10.1016/j.jcf.2018.10.015

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