标题
A new era in the management of Duchenne muscular dystrophy
作者
关键词
-
出版物
DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY
Volume -, Issue -, Pages -
出版商
Wiley
发表日期
2018-12-17
DOI
10.1111/dmcn.14129
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Eteplirsen for paediatric patients with Duchenne muscular dystrophy: A pooled-analysis
- (2018) Liane Randeree et al. JOURNAL OF CLINICAL NEUROSCIENCE
- Diagnosis and management of Duchenne muscular dystrophy, part 3: primary care, emergency management, psychosocial care, and transitions of care across the lifespan
- (2018) David J Birnkrant et al. LANCET NEUROLOGY
- Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and neuromuscular, rehabilitation, endocrine, and gastrointestinal and nutritional management
- (2018) David J Birnkrant et al. LANCET NEUROLOGY
- Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac, bone health, and orthopaedic management
- (2018) David J Birnkrant et al. LANCET NEUROLOGY
- A randomized placebo-controlled phase 3 trial of an antisense oligonucleotide, drisapersen, in Duchenne muscular dystrophy
- (2018) Nathalie Goemans et al. NEUROMUSCULAR DISORDERS
- Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
- (2017) Craig M McDonald et al. LANCET
- Cardiac involvement in the muscular dystrophies
- (2017) Nicholas J. Silvestri et al. MUSCLE & NERVE
- Advances in the Treatment of Duchenne Muscular Dystrophy: New and Emerging Pharmacotherapies
- (2017) Andrea M. Reinig et al. PHARMACOTHERAPY
- Gene therapies that restore dystrophin expression for the treatment of Duchenne muscular dystrophy
- (2016) Jacqueline N. Robinson-Hamm et al. HUMAN GENETICS
- Efficacy of idebenone on respiratory function in patients with Duchenne muscular dystrophy not using glucocorticoids (DELOS): a double-blind randomised placebo-controlled phase 3 trial
- (2015) Gunnar M Buyse et al. LANCET
- Safety and efficacy of drisapersen for the treatment of Duchenne muscular dystrophy (DEMAND II): an exploratory, randomised, placebo-controlled phase 2 study
- (2014) Thomas Voit et al. LANCET NEUROLOGY
- Ataluren treatment of patients with nonsense mutation dystrophinopathy
- (2014) Katharine Bushby et al. MUSCLE & NERVE
- Eteplirsen for the treatment of Duchenne muscular dystrophy
- (2013) Jerry R. Mendell et al. ANNALS OF NEUROLOGY
- Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management
- (2009) Katharine Bushby et al. LANCET NEUROLOGY
- Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care
- (2009) Katharine Bushby et al. LANCET NEUROLOGY
Create your own webinar
Interested in hosting your own webinar? Check the schedule and propose your idea to the Peeref Content Team.
Create NowAsk a Question. Answer a Question.
Quickly pose questions to the entire community. Debate answers and get clarity on the most important issues facing researchers.
Get Started