Feasibility and Safety of Systemic rAAV9-hNAGLU Delivery for Treating Mucopolysaccharidosis IIIB: Toxicology, Biodistribution, and Immunological Assessments in Primates
出版年份 2014 全文链接
标题
Feasibility and Safety of Systemic rAAV9-hNAGLU Delivery for Treating Mucopolysaccharidosis IIIB: Toxicology, Biodistribution, and Immunological Assessments in Primates
作者
关键词
-
出版物
Human Gene Therapy Clinical Development
Volume 25, Issue 2, Pages 72-84
出版商
Mary Ann Liebert Inc
发表日期
2014-04-11
DOI
10.1089/humc.2013.208
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