Strategies for delivery of therapeutics into the central nervous system for treatment of lysosomal storage disorders
出版年份 2012 全文链接
标题
Strategies for delivery of therapeutics into the central nervous system for treatment of lysosomal storage disorders
作者
关键词
-
出版物
Drug Delivery and Translational Research
Volume 2, Issue 3, Pages 169-186
出版商
Springer Nature
发表日期
2012-05-30
DOI
10.1007/s13346-012-0072-4
参考文献
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注意：仅列出部分参考文献，下载原文获取全部文献信息。- Gene Therapy for Lysosomal Storage Diseases (LSDs) in Large Animal Models
- (2013) M. Haskins ILAR JOURNAL
- Intercellular Adhesion Molecule 1 Engagement Modulates Sphingomyelinase and Ceramide, Supporting Uptake of Drug Carriers by the Vascular Endothelium
- (2012) Daniel Serrano et al. ARTERIOSCLEROSIS THROMBOSIS AND VASCULAR BIOLOGY
- Transport of α-Galactosidase Coupled to ICAM-1-Targeted Nanocarriers Across Gastrointestinal Epithelial Cells
- (2012) Rasa Ghaffarian et al. MOLECULAR GENETICS AND METABOLISM
- CNS Penetration of Intrathecal-Lumbar Idursulfase in the Monkey, Dog and Mouse: Implications for Neurological Outcomes of Lysosomal Storage Disorder
- (2012) Pericles Calias et al. PLoS One
- Evaluation of Multivalent, Functional Polymeric Nanoparticles for Imaging Applications
- (2011) Monica Shokeen et al. ACS Nano
- Tight Junctions and Tissue Barriers
- (2011) Ingolf E. Blasig et al. ANTIOXIDANTS & REDOX SIGNALING
- Exosome nanotechnology: An emerging paradigm shift in drug delivery
- (2011) Samira Lakhal et al. BIOESSAYS
- The effect of CD47 modified polymer surfaces on inflammatory cell attachment and activation
- (2011) Stanley J. Stachelek et al. BIOMATERIALS
- Gene Therapy for Lysosomal Storage Diseases: Progress, Challenges and Future Prospects
- (2011) Sergey S. Seregin et al. CURRENT PHARMACEUTICAL DESIGN
- Gene therapy for lysosomal storage disorders
- (2011) Angela Gritti EXPERT OPINION ON BIOLOGICAL THERAPY
- Combination therapies for lysosomal storage disease: is the whole greater than the sum of its parts?
- (2011) J. A. Hawkins-Salsbury et al. HUMAN MOLECULAR GENETICS
- Blood–CNS barrier, neurodegeneration and neuroprotection: recent therapeutic advancements and nano-drug delivery
- (2011) Hari S. Sharma JOURNAL OF NEURAL TRANSMISSION
- Cross-linked antioxidant nanozymes for improved delivery to CNS
- (2011) Natalia L. Klyachko et al. Nanomedicine-Nanotechnology Biology and Medicine
- Minimally invasive molecular delivery into the brain using optical modulation of vascular permeability
- (2011) M. Choi et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Nanoparticles and Colloids as Contributing Factors in Neurodegenerative Disease
- (2011) Stephen C. Bondy International Journal of Environmental Research and Public Health
- Stimuli-Responsive Porous Hydrogels at Interfaces for Molecular Filtration, Separation, Controlled Release, and Gating in Capsules and Membranes
- (2010) Ihor Tokarev et al. ADVANCED MATERIALS
- Pharmacological small molecules for the treatment of lysosomal storage disorders
- (2010) BE Smid et al. EXPERT OPINION ON INVESTIGATIONAL DRUGS
- Recent developments in lipid-based pharmaceutical nanocarriers
- (2010) Tiziana Musacchio Frontiers in Bioscience-Landmark
- Enhanced endothelial delivery and biochemical effects of α-galactosidase by ICAM-1-targeted nanocarriers for Fabry disease
- (2010) Janet Hsu et al. JOURNAL OF CONTROLLED RELEASE
- Optimizing endothelial targeting by modulating the antibody density and particle concentration of anti-ICAM coated carriers
- (2010) Andres J. Calderon et al. JOURNAL OF CONTROLLED RELEASE
- Biopharmaceutical drug targeting to the brain
- (2010) William M. Pardridge JOURNAL OF DRUG TARGETING
- Pathophysiology of neuropathic lysosomal storage disorders
- (2010) Cinzia Maria Bellettato et al. JOURNAL OF INHERITED METABOLIC DISEASE
- Therapeutic approaches for neuronopathic lysosomal storage disorders
- (2010) Raphael Schiffmann JOURNAL OF INHERITED METABOLIC DISEASE
- Protein Modification with Amphiphilic Block Copoly(2-oxazoline)s as a New Platform for Enhanced Cellular Delivery
- (2010) Jing Tong et al. MOLECULAR PHARMACEUTICS
- New biotechnological and nanomedicine strategies for treatment of lysosomal storage disorders
- (2010) Silvia Muro Wiley Interdisciplinary Reviews-Nanomedicine and Nanobiotechnology
- Targeted Delivery of Protein Drugs by Nanocarriers
- (2010) Roberto Solaro et al. Materials
- ICAM-1 targeting of doxorubicin-loaded PLGA nanoparticles to lung epithelial cells
- (2009) Chuda Chittasupho et al. EUROPEAN JOURNAL OF PHARMACEUTICAL SCIENCES
- Intranasal delivery to the central nervous system: Mechanisms and experimental considerations
- (2009) Shyeilla V. Dhuria et al. JOURNAL OF PHARMACEUTICAL SCIENCES
- The Pharmacological Chaperone N-butyldeoxynojirimycin Enhances Enzyme Replacement Therapy in Pompe Disease Fibroblasts
- (2009) Caterina Porto et al. MOLECULAR THERAPY
- CNS-directed gene therapy for lysosomal storage diseases
- (2008) Mark S Sands et al. ACTA PAEDIATRICA
- Substrate reduction therapy
- (2008) Frances M Platt et al. ACTA PAEDIATRICA
- Materials for advanced drug delivery in the 21st century: a focus area for Advanced Drug Delivery Reviews
- (2008) H GHANDEHARI ADVANCED DRUG DELIVERY REVIEWS
- Lysosomal disorders: From storage to cellular damage
- (2008) Andrea Ballabio et al. BIOCHIMICA ET BIOPHYSICA ACTA-MOLECULAR CELL RESEARCH
- Engineering and expression of a chimeric transferrin receptor monoclonal antibody for blood-brain barrier delivery in the mouse
- (2008) Ruben J. Boado et al. BIOTECHNOLOGY AND BIOENGINEERING
- RhoA activation and actin reorganization involved in endothelial CAM-mediated endocytosis of anti-PECAM carriers: critical role for tyrosine 686 in the cytoplasmic tail of PECAM-1
- (2008) C. Garnacho et al. BLOOD
- Oxygen Microscopy by Two-Photon-Excited Phosphorescence
- (2008) Olga S. Finikova et al. CHEMPHYSCHEM
- Getting into the Brain
- (2008) Mayur M Patel et al. CNS DRUGS
- Lysosomal Storage Diseases and the Blood-Brain Barrier
- (2008) David Begley et al. CURRENT PHARMACEUTICAL DESIGN
- Targeted Drugs and Nanomedicine: Present and Future
- (2008) Paul Debbage CURRENT PHARMACEUTICAL DESIGN
- Tailoring the AAV vector capsid for gene therapy
- (2008) L H Vandenberghe et al. GENE THERAPY
- Gateways and tools for drug delivery: Endocytic pathways and the cellular dynamics of cell penetrating peptides
- (2008) Arwyn T. Jones INTERNATIONAL JOURNAL OF PHARMACEUTICS
- Differential intra-endothelial delivery of polymer nanocarriers targeted to distinct PECAM-1 epitopes
- (2008) C GARNACHO et al. JOURNAL OF CONTROLLED RELEASE
- Non-inhibitory antibodies impede lysosomal storage reduction during enzyme replacement therapy of a lysosomal storage disease
- (2008) Ulrich Matzner et al. JOURNAL OF MOLECULAR MEDICINE-JMM
- Delivery of Acid Sphingomyelinase in Normal and Niemann-Pick Disease Mice Using Intercellular Adhesion Molecule-1-Targeted Polymer Nanocarriers
- (2008) C. Garnacho et al. JOURNAL OF PHARMACOLOGY AND EXPERIMENTAL THERAPEUTICS
- Strategies to advance translational research into brain barriers
- (2008) Edward Neuwelt et al. LANCET NEUROLOGY
- Reduced α-Gal A enzyme activity in Fabry fibroblast cells and Fabry mice tissues induced by serum from antibody positive patients with Fabry disease
- (2008) Toya Ohashi et al. MOLECULAR GENETICS AND METABOLISM
- Mannose 6-Phosphate Receptor–mediated Transport of Sulfamidase Across the Blood–brain Barrier in the Newborn Mouse
- (2008) Akihiko Urayama et al. MOLECULAR THERAPY
- Control of Endothelial Targeting and Intracellular Delivery of Therapeutic Enzymes by Modulating the Size and Shape of ICAM-1-targeted Carriers
- (2008) Silvia Muro et al. MOLECULAR THERAPY
- Targeting of the CNS in MPS-IH Using a Nonviral Transferrin-α-l-iduronidase Fusion Gene Product
- (2008) Mark J Osborn et al. MOLECULAR THERAPY
- Cellular uptake and lysosomal delivery of galactocerebrosidase tagged with the HIV Tat protein transduction domain
- (2007) Xian-Yang Zhang et al. JOURNAL OF NEUROCHEMISTRY
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