标题
Perinatal systemic gene delivery using adeno-associated viral vectors
作者
关键词
-
出版物
Frontiers in Molecular Neuroscience
Volume 7, Issue -, Pages -
出版商
Frontiers Media SA
发表日期
2014-11-15
DOI
10.3389/fnmol.2014.00089
参考文献
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Non-invasive prenatal diagnosis: progress and potential
- (2014) Rebecca Daley et al. Archives of Disease in Childhood-Fetal and Neonatal Edition
- Maternal–fetal cellular trafficking
- (2014) Cerine Jeanty et al. CURRENT OPINION IN PEDIATRICS
- Global CNS Transduction of Adult Mice by Intravenously Delivered rAAVrh.8 and rAAVrh.10 and Nonhuman Primates by rAAVrh.10
- (2014) Bin Yang et al. MOLECULAR THERAPY
- Competing for the treasure in exceptions
- (2013) Timothy M. Cox AMERICAN JOURNAL OF HEMATOLOGY
- Initial clinical laboratory experience in noninvasive prenatal testing for fetal aneuploidy from maternal plasma DNA samples
- (2013) Tracy Futch et al. PRENATAL DIAGNOSIS
- The clinical implementation of non-invasive prenatal diagnosis for single-gene disorders: challenges and progress made
- (2013) Nicholas Lench et al. PRENATAL DIAGNOSIS
- Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
- (2013) A. Aiuti et al. SCIENCE
- Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy
- (2013) A. Biffi et al. SCIENCE
- Non-Invasive Chromosomal Evaluation (NICE) Study: results of a multicenter prospective cohort study for detection of fetal trisomy 21 and trisomy 18
- (2012) Mary E. Norton et al. AMERICAN JOURNAL OF OBSTETRICS AND GYNECOLOGY
- The case for intrauterine gene therapy
- (2012) Citra N. Mattar et al. BEST PRACTICE & RESEARCH CLINICAL OBSTETRICS & GYNAECOLOGY
- Noninvasive Prenatal Diagnosis of Monogenic Diseases by Targeted Massively Parallel Sequencing of Maternal Plasma: Application to -Thalassemia
- (2012) K.-W. G. Lam et al. CLINICAL CHEMISTRY
- Systemic delivery of scAAV9 in fetal macaques facilitates neuronal transduction of the central and peripheral nervous systems
- (2012) C N Mattar et al. GENE THERAPY
- Endgame: Glybera Finally Recommended for Approval as the First Gene Therapy Drug in the European Union
- (2012) Seppo Ylä-Herttuala MOLECULAR THERAPY
- Genome-Wide Fetal Aneuploidy Detection by Maternal Plasma DNA Sequencing
- (2012) Diana W. Bianchi et al. OBSTETRICS AND GYNECOLOGY
- Intravenous administration of AAV2/9 to the fetal and neonatal mouse leads to differential targeting of CNS cell types and extensive transduction of the nervous system
- (2011) Ahad A. Rahim et al. FASEB JOURNAL
- Reproducible High Yields of Recombinant Adeno-Associated Virus Produced Using Invertebrate Cells in 0.02- to 200-Liter Cultures
- (2011) Sylvain Cecchini et al. HUMAN GENE THERAPY
- Adeno-Associated Virus Serotype 9 Transduction in the Central Nervous System of Nonhuman Primates
- (2011) Lluis Samaranch et al. HUMAN GENE THERAPY
- Noninvasive Fetal Sex Determination Using Cell-Free Fetal DNA
- (2011) Stephanie A. Devaney et al. JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION
- Preclinical Differences of Intravascular AAV9 Delivery to Neurons and Glia: A Comparative Study of Adult Mice and Nonhuman Primates
- (2011) Steven J Gray et al. MOLECULAR THERAPY
- Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders
- (2011) Adam K Bevan et al. MOLECULAR THERAPY
- Several rAAV Vectors Efficiently Cross the Blood–brain Barrier and Transduce Neurons and Astrocytes in the Neonatal Mouse Central Nervous System
- (2011) Hongwei Zhang et al. MOLECULAR THERAPY
- Correction of Neurological Disease of Mucopolysaccharidosis IIIB in Adult Mice by rAAV9 Trans-Blood–Brain Barrier Gene Delivery
- (2011) Haiyan Fu et al. MOLECULAR THERAPY
- Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B
- (2011) Amit C. Nathwani et al. NEW ENGLAND JOURNAL OF MEDICINE
- In uterogene transfer to the mouse nervous system: Figure 1
- (2010) Ahad A. Rahim et al. BIOCHEMICAL SOCIETY TRANSACTIONS
- Type 2 Gaucher disease: Phenotypic variation and genotypic heterogeneity
- (2010) N. Gupta et al. BLOOD CELLS MOLECULES AND DISEASES
- Prevalence of Serum IgG and Neutralizing Factors Against Adeno-Associated Virus (AAV) Types 1, 2, 5, 6, 8, and 9 in the Healthy Population: Implications for Gene Therapy Using AAV Vectors
- (2010) Sylvie Boutin et al. HUMAN GENE THERAPY
- Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN
- (2010) Kevin D Foust et al. NATURE BIOTECHNOLOGY
- Maternal Plasma DNA Sequencing Reveals the Genome-Wide Genetic and Mutational Profile of the Fetus
- (2010) Y. M. D. Lo et al. Science Translational Medicine
- The clinical spectrum of fetal Niemann-Pick type C
- (2009) Ronen Spiegel et al. AMERICAN JOURNAL OF MEDICAL GENETICS PART A
- Maternal alloantibodies induce a postnatal immune response that limits engraftment following in utero hematopoietic cell transplantation in mice
- (2009) Demetri J. Merianos et al. JOURNAL OF CLINICAL INVESTIGATION
- Improved Metabolic Correction in Patients with Lysosomal Storage Disease Treated with Hematopoietic Stem Cell Transplant Compared with Enzyme Replacement Therapy
- (2009) Robert F. Wynn et al. JOURNAL OF PEDIATRICS
- Intravenous Administration of Self-complementary AAV9 Enables Transgene Delivery to Adult Motor Neurons
- (2009) Sandra Duque et al. MOLECULAR THERAPY
- Characterization of Genome Integrity for Oversized Recombinant AAV Vector
- (2009) Biao Dong et al. MOLECULAR THERAPY
- Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
- (2009) N. Cartier et al. SCIENCE
- Gene Therapy Using Adeno-Associated Virus Vectors
- (2008) S. Daya et al. CLINICAL MICROBIOLOGY REVIEWS
- Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients
- (2008) Steven J. Howe et al. JOURNAL OF CLINICAL INVESTIGATION
- Systemic AAV6 Delivery Mediating RNA Interference Against SOD1: Neuromuscular Transduction Does Not Alter Disease Progression in fALS Mice
- (2008) Chris Towne et al. MOLECULAR THERAPY
- Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection
- (2008) Carmela Zincarelli et al. MOLECULAR THERAPY
- Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes
- (2008) Kevin D Foust et al. NATURE BIOTECHNOLOGY
- Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis
- (2008) James W.B. Bainbridge et al. NEW ENGLAND JOURNAL OF MEDICINE
- Noninvasive diagnosis of fetal aneuploidy by shotgun sequencing DNA from maternal blood
- (2008) H. C. Fan et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Gene therapy for the fetus: is there a future?
- (2007) Anna L. David et al. BEST PRACTICE & RESEARCH CLINICAL OBSTETRICS & GYNAECOLOGY
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