标题
Statistical Challenges in the Evaluation of Treatments for Small Patient Populations
作者
关键词
-
出版物
Science Translational Medicine
Volume 5, Issue 178, Pages 178sr3-178sr3
出版商
American Association for the Advancement of Science (AAAS)
发表日期
2013-03-28
DOI
10.1126/scitranslmed.3004018
参考文献
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Adaptive Randomization Versus Interim Monitoring
- (2013) Boris Freidlin et al. JOURNAL OF CLINICAL ONCOLOGY
- Sustained response and prevention of damage progression in patients with neonatal-onset multisystem inflammatory disease treated with anakinra: A cohort study to determine three- and five-year outcomes
- (2012) Cailin H. Sibley et al. ARTHRITIS AND RHEUMATISM
- Design Issues in Randomized Phase II/III Trials
- (2012) Edward L. Korn et al. JOURNAL OF CLINICAL ONCOLOGY
- Prospective Trial of a Pediatric Ventricular Assist Device
- (2012) Charles D. Fraser et al. NEW ENGLAND JOURNAL OF MEDICINE
- Clinical trial of a farnesyltransferase inhibitor in children with Hutchinson-Gilford progeria syndrome
- (2012) L. B. Gordon et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Berlin Heart EXCOR Pediatric ventricular assist device Investigational Device Exemption study: Study design and rationale
- (2011) Christopher S. Almond et al. AMERICAN HEART JOURNAL
- Reply to M. Buyse et al
- (2011) Edward L. Korn et al. JOURNAL OF CLINICAL ONCOLOGY
- Reply to Y. Yuan et al
- (2011) Edward L. Korn et al. JOURNAL OF CLINICAL ONCOLOGY
- Overall Survival As the Outcome for Randomized Clinical Trials With Effective Subsequent Therapies
- (2011) Edward L. Korn et al. JOURNAL OF CLINICAL ONCOLOGY
- A CFTR Potentiator in Patients with Cystic Fibrosis and theG551DMutation
- (2011) Bonnie W. Ramsey et al. NEW ENGLAND JOURNAL OF MEDICINE
- Testing and interval estimation for two-sample survival comparisons with small sample sizes and unequal censoring
- (2010) Rui Wang et al. BIOSTATISTICS
- Efficacy and tolerability of a new formulation of pancrelipase delayed-release capsules in children aged 7 to 11 years with exocrine pancreatic insufficiency and cystic fibrosis: A multicenter, randomized, double-blind, placebo-controlled, two-period crossover, superiority study
- (2010) Gavin R. Graff et al. CLINICAL THERAPEUTICS
- A general inefficacy interim monitoring rule for randomized clinical trials
- (2010) Boris Freidlin et al. Clinical Trials
- Outcome-Adaptive Randomization: Is It Useful?
- (2010) Edward L. Korn et al. JOURNAL OF CLINICAL ONCOLOGY
- Trastuzumab in combination with chemotherapy versus chemotherapy alone for treatment of HER2-positive advanced gastric or gastro-oesophageal junction cancer (ToGA): a phase 3, open-label, randomised controlled trial
- (2010) Yung-Jue Bang et al. LANCET
- Effect of VX-770 in Persons with Cystic Fibrosis and the G551D-CFTRMutation
- (2010) Frank J. Accurso et al. NEW ENGLAND JOURNAL OF MEDICINE
- Anaplastic Lymphoma Kinase Inhibition in Non–Small-Cell Lung Cancer
- (2010) Eunice L. Kwak et al. NEW ENGLAND JOURNAL OF MEDICINE
- The Path to Personalized Medicine
- (2010) Margaret A. Hamburg et al. NEW ENGLAND JOURNAL OF MEDICINE
- Effective Incorporation of Biomarkers into Phase II Trials
- (2009) L. M. McShane et al. CLINICAL CANCER RESEARCH
- Improved Early Event-Free Survival With Imatinib in Philadelphia Chromosome–Positive Acute Lymphoblastic Leukemia: A Children's Oncology Group Study
- (2009) Kirk R. Schultz et al. JOURNAL OF CLINICAL ONCOLOGY
- Multi-Arm Clinical Trials of New Agents: Some Design Considerations
- (2008) B. Freidlin et al. CLINICAL CANCER RESEARCH
- Monitoring for Lack of Benefit: A Critical Component of a Randomized Clinical Trial
- (2008) Boris Freidlin et al. JOURNAL OF CLINICAL ONCOLOGY
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