Nasal Administration of Cationic Nanoemulsions as Nucleic Acids Delivery Systems Aiming at Mucopolysaccharidosis Type I Gene Therapy
出版年份 2018 全文链接
标题
Nasal Administration of Cationic Nanoemulsions as Nucleic Acids Delivery Systems Aiming at Mucopolysaccharidosis Type I Gene Therapy
作者
关键词
-
出版物
PHARMACEUTICAL RESEARCH
Volume 35, Issue 11, Pages -
出版商
Springer Nature America, Inc
发表日期
2018-09-27
DOI
10.1007/s11095-018-2503-5
参考文献
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Gene editing of MPS I human fibroblasts by co-delivery of a CRISPR/Cas9 plasmid and a donor oligonucleotide using nanoemulsions as nonviral carriers
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