标题
Miglustat in Niemann-Pick disease type C patients: a review
作者
关键词
Niemann-Pick disease type C, Miglustat, Efficacy, Biomarker
出版物
Orphanet Journal of Rare Diseases
Volume 13, Issue 1, Pages -
出版商
Springer Nature America, Inc
发表日期
2018-08-15
DOI
10.1186/s13023-018-0844-0
参考文献
相关参考文献
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