标题
Spinal muscular atrophy
作者
关键词
-
出版物
Orphanet Journal of Rare Diseases
Volume 6, Issue 1, Pages 71
出版商
Springer Nature
发表日期
2011-11-03
DOI
10.1186/1750-1172-6-71
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Early Functional Impairment of Sensory-Motor Connectivity in a Mouse Model of Spinal Muscular Atrophy
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- Seize the day: Newborn screening for SMA
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- SAHA ameliorates the SMA phenotype in two mouse models for spinal muscular atrophy
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- Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice
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- Induced Pluripotent Stem Cells Generated from Patients with ALS Can Be Differentiated into Motor Neurons
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