A Bicyclic 1-Deoxygalactonojirimycin Derivative as a Novel Pharmacological Chaperone for GM1 Gangliosidosis

标题
A Bicyclic 1-Deoxygalactonojirimycin Derivative as a Novel Pharmacological Chaperone for GM1 Gangliosidosis
作者
关键词
-
出版物
MOLECULAR THERAPY
Volume 21, Issue 3, Pages 526-532
出版商
Elsevier BV
发表日期
2013-01-22
DOI
10.1038/mt.2012.263

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