标题
Treatment of lysosomal storage disorders: successes and challenges
作者
关键词
Hematopoietic Stem Cell Transplantation, Enzyme Replacement Therapy, Fabry Disease, Gauche Disease, Central Nervous System Disease
出版物
JOURNAL OF INHERITED METABOLIC DISEASE
Volume 37, Issue 4, Pages 587-598
出版商
Springer Nature
发表日期
2014-05-12
DOI
10.1007/s10545-014-9718-3
参考文献
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