Postsymptomatic restoration of SMN rescues the disease phenotype in a mouse model of severe spinal muscular atrophy
出版年份 2011 全文链接
标题
Postsymptomatic restoration of SMN rescues the disease phenotype in a mouse model of severe spinal muscular atrophy
作者
关键词
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出版物
JOURNAL OF CLINICAL INVESTIGATION
Volume 121, Issue 8, Pages 3029-3041
出版商
American Society for Clinical Investigation
发表日期
2011-07-25
DOI
10.1172/jci57291
参考文献
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model
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