Moving forward: cystic fibrosis gene therapy

Expert opinion in biological therapy: update on developments in lung gene transfer

(2013) Uta Griesenbach et al.   EXPERT OPINION ON BIOLOGICAL THERAPY

CpG-depleted adeno-associated virus vectors evade immune detection

(2013) Susan M. Faust et al.   JOURNAL OF CLINICAL INVESTIGATION

High efficiency gene transfer to airways of mice using influenza hemagglutinin pseudotyped lentiviral vectors

(2013) Manij Patel et al.   JOURNAL OF GENE MEDICINE

Adenoviral Gene Transfer Corrects the Ion Transport Defect in the Sinus Epithelia of a Porcine CF Model

(2013) Andrea E Potash et al.   MOLECULAR THERAPY

Assessment of F/HN-Pseudotyped Lentivirus as a Clinically Relevant Vector for Lung Gene Therapy

(2012) Uta Griesenbach et al.   AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE

The use of CpG-free plasmids to mediate persistent gene expression following repeated aerosol delivery of pDNA/PEI complexes

(2012) Lee A. Davies et al.   BIOMATERIALS

Progress in Gene and Cell Therapy for Cystic Fibrosis Lung Disease

(2012) Uta Griesenbach et al.   CURRENT PHARMACEUTICAL DESIGN

Lentiviral Vector Gene Transfer to Porcine Airways

(2012) Patrick L Sinn et al.   Molecular Therapy-Nucleic Acids

Gene therapy finds its niche

(2011) Cormac Sheridan   NATURE BIOTECHNOLOGY

Chemical vectors for gene delivery: uptake and intracellular trafficking

(2010) Chantal Pichon et al.   CURRENT OPINION IN BIOTECHNOLOGY

Toward Gene Therapy for Cystic Fibrosis Using a Lentivirus Pseudotyped With Sendai Virus Envelopes

(2010) Katsuyuki Mitomo et al.   MOLECULAR THERAPY

Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease

(2010) Stefan Stein et al.   NATURE MEDICINE

Disease-causing Mutations in the Cystic Fibrosis Transmembrane Conductance Regulator Determine the Functional Responses of Alveolar Macrophages

(2009) Ludmila V. Deriy et al.   JOURNAL OF BIOLOGICAL CHEMISTRY

Single-dose lentiviral gene transfer for lifetime airway gene expression

(2009) Alice G. Stocker et al.   JOURNAL OF GENE MEDICINE

CFTR Delivery to 25% of Surface Epithelial Cells Restores Normal Rates of Mucus Transport to Human Cystic Fibrosis Airway Epithelium

(2009) Liqun Zhang et al.   PLOS BIOLOGY

Gene transfer to the lung: Lessons learned from more than 2 decades of CF gene therapy

(2008) Uta Griesenbach et al.   ADVANCED DRUG DELIVERY REVIEWS

Extracellular barriers in respiratory gene therapy

(2008) Niek Sanders et al.   ADVANCED DRUG DELIVERY REVIEWS

Progress and prospects: gene therapy for genetic diseases with helper-dependent adenoviral vectors

(2008) N Brunetti-Pierri et al.   GENE THERAPY

Lentivirus Vector Can Be Readministered to Nasal Epithelia without Blocking Immune Responses

(2008) P. L. Sinn et al.   JOURNAL OF VIROLOGY

Analysis of Adeno-associated Virus Progenitor Cell Transduction in Mouse Lung

(2008) Xiaoming Liu et al.   MOLECULAR THERAPY

Transduction Efficiencies of Novel AAV Vectors in Mouse Airway Epithelium In Vivo and Human Ciliated Airway Epithelium In Vitro

(2008) Maria P Limberis et al.   MOLECULAR THERAPY

CpG-free plasmids confer reduced inflammation and sustained pulmonary gene expression

(2008) Stephen C Hyde et al.   NATURE BIOTECHNOLOGY