标题
Gene therapy for leukodystrophies
作者
关键词
-
出版物
HUMAN MOLECULAR GENETICS
Volume 20, Issue R1, Pages R42-R53
出版商
Oxford University Press (OUP)
发表日期
2011-04-02
DOI
10.1093/hmg/ddr142
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Leukodystrophy and Gene Therapy with a Dimmer Switch
- (2011) Paul J. Orchard et al. NEW ENGLAND JOURNAL OF MEDICINE
- The galactocerebrosidase enzyme contributes to the maintenance of a functional hematopoietic stem cell niche
- (2010) I. Visigalli et al. BLOOD
- Gene therapy for late infantile neuronal ceroid lipofuscinosis: neurosurgical considerations
- (2010) Mark M. Souweidane et al. Journal of Neurosurgery-Pediatrics
- Gene delivery of AAV2-neurturin for Parkinson's disease: a double-blind, randomised, controlled trial
- (2010) William J Marks et al. LANCET NEUROLOGY
- Differential Adeno-Associated Virus Mediated Gene Transfer to Sensory Neurons following Intrathecal Delivery by Direct Lumbar Puncture
- (2010) Lucy Vulchanova et al. Molecular Pain
- Myelination and support of axonal integrity by glia
- (2010) Klaus-Armin Nave NATURE
- The myeloid cells of the central nervous system parenchyma
- (2010) Richard M. Ransohoff et al. NATURE
- Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
- (2010) Marina Cavazzana-Calvo et al. NATURE
- Microglia in neurodegenerative disease
- (2010) V. Hugh Perry et al. Nature Reviews Neurology
- Changing Face of Microglia
- (2010) M. B. Graeber SCIENCE
- Fate Mapping Analysis Reveals That Adult Microglia Derive from Primitive Macrophages
- (2010) F. Ginhoux et al. SCIENCE
- Identification of Hematopoietic Stem Cell-Specific miRNAs Enables Gene Therapy of Globoid Cell Leukodystrophy
- (2010) B. Gentner et al. Science Translational Medicine
- Genetically Modified CD34+ Hematopoietic Stem Cells Contribute to Turnover of Brain Perivascular Macrophages in Long-Term Repopulated Primates
- (2009) Caroline Soulas et al. AMERICAN JOURNAL OF PATHOLOGY
- Leukodystrophies and other genetic metabolic leukoencephalopathies in children and adults
- (2009) Alfried Kohlschütter et al. BRAIN & DEVELOPMENT
- Efficient intracerebral delivery of AAV5 vector encoding human ARSA in non-human primate
- (2009) M.-A. Colle et al. HUMAN MOLECULAR GENETICS
- The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy
- (2009) Eugenio Montini et al. JOURNAL OF CLINICAL INVESTIGATION
- Enzyme Replacement Improves Ataxic Gait and Central Nervous System Histopathology in a Mouse Model of Metachromatic Leukodystrophy
- (2009) Ulrich Matzner et al. MOLECULAR THERAPY
- Molecular Evolution of Adeno-associated Virus for Enhanced Glial Gene Delivery
- (2009) James T Koerber et al. MOLECULAR THERAPY
- Molecular signatures of disease brain endothelia provide new sites for CNS-directed enzyme therapy
- (2009) Yong Hong Chen et al. NATURE MEDICINE
- Safety and tolerability of putaminal AADC gene therapy for Parkinson disease
- (2009) C. W. Christine et al. NEUROLOGY
- Invited Article: An MRI-based approach to the diagnosis of white matter disorders
- (2009) R. Schiffmann et al. NEUROLOGY
- Efficient gene therapy-based method for the delivery of therapeutics to primate cortex
- (2009) A. P. Kells et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
- (2009) N. Cartier et al. SCIENCE
- Dopamine Gene Therapy for Parkinson's Disease in a Nonhuman Primate Without Associated Dyskinesia
- (2009) B. Jarraya et al. Science Translational Medicine
- Is microglial apoptosis an early pathogenic change in cerebral X-linked adrenoleukodystrophy?
- (2008) Florian S. Eichler et al. ANNALS OF NEUROLOGY
- Axon-Glial Signaling and the Glial Support of Axon Function
- (2008) Klaus-Armin Nave et al. Annual Review of Neuroscience
- Genes involved in leukodystrophies: A glance at glial functions
- (2008) Odile Boespflug-Tanguy et al. Current Neurology and Neuroscience Reports
- Treatment of Late Infantile Neuronal Ceroid Lipofuscinosis by CNS Administration of a Serotype 2 Adeno-Associated Virus Expressing CLN2 cDNA
- (2008) Stefan Worgall et al. HUMAN GENE THERAPY
- Early oxidative damage underlying neurodegeneration in X-adrenoleukodystrophy
- (2008) S. Fourcade et al. HUMAN MOLECULAR GENETICS
- Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
- (2008) Salima Hacein-Bey-Abina et al. JOURNAL OF CLINICAL INVESTIGATION
- The role of AMPK in psychosine mediated effects on oligodendrocytes and astrocytes: implication for Krabbe Disease
- (2008) Shailendra Giri et al. JOURNAL OF NEUROCHEMISTRY
- Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes
- (2008) Kevin D Foust et al. NATURE BIOTECHNOLOGY
- Remyelination in the CNS: from biology to therapy
- (2008) Robin J. M. Franklin et al. NATURE REVIEWS NEUROSCIENCE
- Dysfunctional astrocytes as key players in the pathogenesis of central nervous system disorders
- (2007) Jacques De Keyser et al. JOURNAL OF THE NEUROLOGICAL SCIENCES
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