A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice
出版年份 2013 全文链接
标题
A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice
作者
关键词
-
出版物
HUMAN GENE THERAPY
Volume 24, Issue 3, Pages 331-342
出版商
Mary Ann Liebert Inc
发表日期
2013-01-23
DOI
10.1089/hum.2012.211
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