标题
In Utero Enzyme-Replacement Therapy for Infantile-Onset Pompe’s Disease
作者
关键词
-
出版物
NEW ENGLAND JOURNAL OF MEDICINE
Volume 387, Issue 23, Pages 2150-2158
出版商
Massachusetts Medical Society
发表日期
2022-11-10
DOI
10.1056/nejmoa2200587
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction
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